NorthStar Clinical Studies

Northstar Clinical Studies Underway

The Northstar Studies are global clinical studies being conducted to determine if the one-time gene therapy can decrease or eliminate the need for continued blood transfusions in people living with transfusion-dependent beta-thalassemia, while also being safe and well-tolerated.

Northstar-2 Study Now Enrolling

The study now enrolling, Northstar-2, is a Phase 3 global clinical study seeking to enroll patients who cannot make enough of the beta-globin portion of hemoglobin. See if someone you know may qualify.